An expert involved in the first successful gene therapy trial for Huntington's Disease discusses the trial results and ...

Huntington's disease is a devastating brain disorder that slowly robs people of movement, memory, and personality. It is ...

Treatments that target a fragment of the mutant protein that causes Huntington's disease might be more effective than ...

Findings from preclinical studies could point to therapeutic strategies for Huntington’s disease, as well as other neurodegenerative disorders and potentially cancer.

While the FDA appears to be adamant that uniQure conduct a sham surgery–controlled Phase 3 trial before AMT-130 can be considered for approval, experts believe there is an alternate path forward for ...

Add Yahoo as a preferred source to see more of our stories on Google. Gene therapy is becoming a powerful way to treat challenging diseases that don’t respond to traditional treatments, and ...

ST. LOUIS — Scientists may have reached a breakthrough in the fight against Huntington’s disease, a rare and fatal inherited brain disorder with no cure. For the first time, a gene therapy has been ...

For the first time, scientists have successfully treated someone suffering from Huntington's disease, a fatal genetic illness ...

UCL and uniQure report the first treatment to slow Huntington’s disease with gene therapy AMT-130. High-dose patients had 75% less progression over three years compared with standard care. uniQure ...

The first signs of Huntington’s disease are often subtle changes in coordination, such as clumsiness or trouble with balance. You may also begin to notice changes in thinking, such as difficulty ...