COLUMBUS, Ohio (WCMH) – It’s being called a pioneering event that holds great promise for children who have Duchenne muscular dystrophy. After decades of research, animal studies, and human trials, ...

"The most apparent take-away from the study findings is that a model of developmental therapy focusing on frequency, intensity, and variability of activity, exercise, and self-driven exploration may ...

The first gene therapy for children with Duchenne muscular dystrophy has been approved by the U.S. Food and Drug Administration. The therapy can be used in 4- and 5-year-olds with the degenerative ...

COLORADO SPRINGS, Colo. (KRDO) -- A groundbreaking gene therapy was recently approved by the U.S. Food and Drug Administration to treat the most common form of muscular dystrophy in children, Duchenne ...

Gene therapies have extended survival in muscular dystrophy, requiring improved care transitions from pediatric to adult systems. Current systems lack adequate staffing, specialists, and communication ...

Waking up, hopping out of the bed, and stumbling to the kitchen for a cup of coffee: It’s an everyday routine most people don’t think twice about. But for children with spinal muscular atrophy, simply ...