Ring Therapeutics’ hunt for new human viruses that can deliver gene therapies multiple times in a single patient appears to have landed on a viable candidate, new mouse data have suggested. In a ...

Speaking at the ELRIG meeting at Hinxton Hall in March, Dr Seng H. Cheng set out how next-generation adeno-associated viral ...

The researchers say that, to their knowledge, this is the first demonstration of programmable, site-specific integration of a ...

Researchers have found that a new base-editing gene therapy can help treat a rare neurodevelopmental disorder called Snijders Blok–Campeau syndrome caused by mutations in the CHD3 gene. A specialized ...

Now, researchers have developed a noninvasive method of delivering CRISPR/Cas9 gene editing technology to the brain to knock out a gene associated with anxiety and depression in mice. They say it’s ...

Mice and newts were applied to the one-step Cre-loxP organism creation technology by TAx9. In this study, the researchers succeeded in synthesizing a Cre-loxP integrated vector by placing a short DNA ...

Zheng-Yi Chen, DPhil, associate scientist at the Eaton-Peabody Laboratories, and Ines and Fredrick Yeatts Chair in Otolaryngology, at Mass Eye and Ear, is the senior and co-corresponding author of a ...